When a $2.1 Million Drug Could Cure Your Child’s Fatal Disease
Gene therapy is bringing out the best in America’s health-care system—and its worst.
Zolgensma, the first systemic gene therapy of its kind that the U.S. Food and Drug Administration has approved, appears to cure in one shot a rare muscle-destroying disease that can be a death sentence for infants and toddlers.
It’s also the world’s most expensive medication. Novartis AG set the price at $2.1 million after the FDA approval came down on May 24, and some families have been left scrambling for ways to get the drug in its first several months on the market.
https://www.bloomberg.com/news/features/2019-08-20/how-parents-get-zolgensma-the-world-s-most-expensive-drug?srnd=businessweek-v2